Browsing by Author Gómez Grau, Marta
Showing results 1 to 2 of 2
Issue Date | Title | Author(s) |
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19-Aug-2015 | Evaluation of aminoglycoside and non-aminoglycoside compounds for stop-codon readthrough therapy in four lysosomal storage diseases | Gómez Grau, Marta; Garrido Fernández, Elena; Cozar, Mónica; Rodríguez Sureda, Víctor; Domínguez, Carmen; Arenas Solà, Concepción; Gatti, Richard A; Cormand Rifà, Bru; Grinberg Vaisman, Daniel Raúl; Vilageliu i Arqués, Lluïsa |
7-Feb-2017 | New murine Niemann-Pick type C models bearing a pseudoexongenerating mutation recapitulate the main neurobehavioural and molecular features of the disease | Gómez Grau, Marta; Albaigès, Júlia; Casas, Josefina; Auladell i Costa, M. Carme; Dierssen, Mara; Vilageliu i Arqués, Lluïsa; Grinberg Vaisman, Daniel Raúl |