Browsing by Author Canals Montferrer, Isaac

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Showing results 7 to 9 of 9 < previous 
Issue DateTitleAuthor(s)
28-Feb-2020Neuronal and astrocytic differentiation from Sanfilippo C syndrome iPSCs for disease modeling and drug developmentBenetó, Noelia; Cozar, Mónica; Castilla-Vallmanya, Laura; Zetterdahl, Oskar G.; Sacultanu, Madalina; Segur-Bailach, Eulalia; García-Morant, María; Ribes, Antonia; Ahlenius, Henrik; Grinberg Vaisman, Daniel Raúl; Vilageliu i Arqués, Lluïsa; Canals Montferrer, Isaac
22-Oct-2020Sanfilippo syndrome: molecular basis, disease models and therapeutic approachesBenetó, Noelia; Vilageliu i Arqués, Lluïsa; Grinberg Vaisman, Daniel Raúl; Canals Montferrer, Isaac
24-Dec-2014Therapeutic strategies based on modified U1 snRNAs and chaperones for Sanfilippo C splicing mutationsMatos, Liliana; Canals Montferrer, Isaac; Dridi, Larbi; Choi, Yoo; Prata, Maria Joao; Jordan, Peter; Desviat, Lourdes R.; Pérez, Belén; Pshezhetsky, Alexey V.; Grinberg Vaisman, Daniel Raúl; Alves, Sandra; Vilageliu i Arqués, Lluïsa