Browsing by Author Canals Montferrer, Isaac
Showing results 8 to 9 of 9
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Issue Date | Title | Author(s) |
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22-Oct-2020 | Sanfilippo syndrome: molecular basis, disease models and therapeutic approaches | Benetó, Noelia; Vilageliu i Arqués, Lluïsa; Grinberg Vaisman, Daniel Raúl; Canals Montferrer, Isaac |
24-Dec-2014 | Therapeutic strategies based on modified U1 snRNAs and chaperones for Sanfilippo C splicing mutations | Matos, Liliana; Canals Montferrer, Isaac; Dridi, Larbi; Choi, Yoo; Prata, Maria Joao; Jordan, Peter; Desviat, Lourdes R.; Pérez, Belén; Pshezhetsky, Alexey V.; Grinberg Vaisman, Daniel Raúl; Alves, Sandra; Vilageliu i Arqués, Lluïsa |