Browsing by Author Barbon, Elena
Showing results 1 to 1 of 1
Issue Date | Title | Author(s) |
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2024 | Treatment of Infantile-Onset Pompe Disease in a Rat Model with Muscle-Directed AAV Gene Therapy | El Andari, Jihad; Muñoz, Sergio; Bertolín, Joan; Jiménez Perales, Verónica; Jaén, Maria Luisa; Garcia, Miquel; Pujol, Anna; Vilà Prats, Laia; Sacristán, Víctor; Barbon, Elena; Ronzitti, Giuseppe; Tulalamba, Warut; Pham, Quang Hong; Ruberte París, Jesús; Vanden Driessche, Thierry; Chuah, Marinee K.; Grimm, Dirk; Mingozzi, Federico; Bosch i Tubert, Fàtima |