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9-gen-2024Tetrahydrobiopterin (BH4) treatment stabilizes tyrosine hydroxylase: Rescue of tyrosine hydroxylase deficiency phenotypes in human neurons and in a knock-in mouse modelKunwar, Jung-KC; Tristán Noguero, Alba; Altankhuyag, Altanchimeg; Piñol Belenguer, David; Prestegård, Karina S.; Fernández Carasa, Irene; Colini Baldeschi, Arianna; Sigatullina Bondarenko, Maria; García-Cazorla, Angeles; Consiglio, Antonella; Martinez, Aurora