Browsing by Author Mingozzi, Federico
Showing results 1 to 2 of 2
Issue Date | Title | Author(s) |
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2024 | Treatment of Infantile-Onset Pompe Disease in a Rat Model with Muscle-Directed AAV Gene Therapy | El Andari, Jihad; Muñoz, Sergio; Bertolín, Joan; Jiménez Perales, Verónica; Jaén, Maria Luisa; Garcia, Miquel; Pujol, Anna; Vilà Prats, Laia; Sacristán, Víctor; Barbon, Elena; Ronzitti, Giuseppe; Tulalamba, Warut; Pham, Quang Hong; Ruberte París, Jesús; Vanden Driessche, Thierry; Chuah, Marinee K.; Grimm, Dirk; Mingozzi, Federico; Bosch i Tubert, Fàtima |
1-Jul-2013 | Whole body correction of mucopolysaccharidosis IIIA by intracerebrospinal fluid gene therapy | Bosch i Tubert, Fàtima; Haurigot, Virginia; Marcó, Sara; Ribera, Albert; García Martínez, Miguel; Ruzo, Albert; Villacampa, Pilar; Ayuso, Eduard; Añor Torres, Sònia; Andaluz Martínez, Anna; Pineda, Mercedes; García-Fructuoso, Gemma; Molas Laplana, Maria; Maggioni, Luca; Muñoz, Sergio; Motas, Sandra; Ruberte París, Jesús; Mingozzi, Federico; Pumarola i Batlle, Martí |