Browsing by Subject Gene therapy

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Issue DateTitleAuthor(s)
25-Jul-2019A pharmacogenetic intervention for the improvement of the safety profile of antipsychotic treatmentsArranz, María Jesús; González Rodríguez, Alexandre; Pérez Blanco, Josefina; Penadés Rubio, Rafael; Gutiérrez, Blanca; Ibáñez Lladó, Laura; Arias Sampériz, Bárbara; Brunet i Serra, Mercè; Cervilla, Jorge; Salazar, Juliana; Catalán, Rosa
28-Apr-2023Administration of chitosan-tripolyphosphate-DNA nanoparticles overexpressing key enzymes to improve omega-3 long-chain polyunsaturated fatty acid synthesis in gilthead sea bream (Sparus aurata)Wu, Yuanbing
6-Sep-2018Administration of chitosan-tripolyphosphate-DNA nanoparticles to knockdown glutamate dehydrogenase expression impairs transdeamination and gluconeogenesis in the liverGaspar Condori, Juan Carlos; Silva-Marrero, Jonás I.; Fábregas, A. (Anna); Miñarro Carmona, Montserrat; Ticó Grau, Josep R.; Vázquez Baanante, Ma. Isabel; Metón Teijeiro, Isidoro
25-Nov-2016Aminocyclitol and iminosugar derivatives related to Gauche diseaseMonlleó Mas, Ester
24-Jun-2021Anti-TGFβ (Transforming Growth Factor β) Therapy With Betaglycan-Derived P144 Peptide Gene Delivery Prevents the Formation of Aortic Aneurysm in a Mouse Model of Marfan SyndromeArce, Cristina; Rodríguez Rovira, Isaac; De Rycke, Karo; Durán, Karina; Campuzano Uceda, María Victoria; Fabregat Romero, Isabel; Jiménez Altayó, Francesc; Berraondo, Pedro; Egea Guri, Gustavo
7-Oct-2011Aproximació terapèutica per a la malaltia de Gaucher basada en xaperonesSànchez Ollé, Gessamí
8-Jun-2009Augment de l'eficàcia antitumoral d'adenovirus replicatius mitjançant l'expressió de hialuronidasa i proteïnes fusogéniques de membranaGuedán Carrió, Sònia
11-Jan-2021Biomedical applications of PolyPurine Reverse Hoogsteen hairpins: immunotherapy and gene repairJiménez Félix, Alejandro
6-Nov-2018Cancer immunotherapy using polypurine reverse hoogsteen hairpins targeting the PD-1/PD-L1 pathway in human tumor cells.Medina Enríquez, Miriam Marlene; Félix, Álex J.; Ciudad i Gómez, Carlos Julián; Noé Mata, Verónica
31-Mar-2006Caracterització de mutacions causants de la malaltia de Gaucher. Aproximació a una teràpia gènica.Diaz Font, Anna
19-Nov-2020Cell Banking of HEK293T cell line for clinical-grade lentiviral particles manufacturingPerpiñá Martin, Unai; Herranz, Cristina; Martín Ibáñez, Raquel; Boronat Barado, Anna; Chiappe, Felipe; Monforte, Verónica; Orpella Aceret, Gemma; González, Ester; Olivé, Myriam; Castella, Maria; Suñé, Guillermo; Urbano Ispizua, Álvaro; Delgado, Julio (Delgado González); Juan, Manel; Canals i Coll, Josep M.
5-May-2020Cerebellar astrocyte transduction as gene therapy for megalencephalic leukoencephalopathySánchez, Ángela; García-Lareu, Belén; Puig, Meritxell; Prat, Esther; Ruberte París, Jesús; Chillón, Miguel; Nunes Martínez, Virginia; Estévez Povedano, Raúl; Bosch, Assumpció
19-Apr-2024CERKL as a modulator gene of mitochondrial dynamics and stress response in the retinaGarcía Arroyo, Rocío
28-Nov-2008Cèl·lules mare mesenquimàtiques humanes derivades de teixit adipós per a la teràpia cel·lular. Seguiment "in vivo" mitjançant procediments d'imatge no invasius.Vilalta Colomer, Marta
1-Nov-2011Characterization of human pancreatic orthotopic tumor xenografts suitable for drug screeningPérez Torras, Sandra; Vidal Pla, Anna; Miquel Morera, Rosa; Almendro Navarro, Vanessa; Fernández-Cruz, Laureano; Navarro Colás, Salvador; Maurel Santasusana, Joan; Carbó Carbó, Neus; Gascón, Pere; Mazo Sánchez, Adela
Mar-2019Chimeric Antigen Receptor T-cell Therapy: Bioengineered immunocellular approach to Acute Lymphoblastic LeukaemiaBachiller García, Mireia
21-May-2020Chitosan-Based Drug Delivery System: Applications in Fish BiotechnologyWu, Yuanbing; Rashidpour, Ania; Almajano Pablos, Ma. Pilar (María Pilar); Metón Teijeiro, Isidoro
Feb-2016Chitosan-mediated shRNA knockdown of cytosolic alanine aminotransferase improves hepatic carbohydrate metabolismGonzález, Juan D.; Silva-Marrero, Jonás I.; Metón Teijeiro, Isidoro; Caballero Solares, Albert; Viegas, Iván; Fernández González, Felipe Javier; Miñarro Carmona, Montserrat; Fábregas, A. (Anna); Ticó Grau, Josep R.; Jones, John G.; Vázquez Baanante, Ma. Isabel
12-Jul-2019Cholesteryl oleate-loaded solid lipid nanoparticles for the vectorization of nucleic acidsSuñé Pou, Marc
9-Nov-2023Comparative Analysis of the Physicochemical and Biological Characteristics of Freeze-Dried PEGylated Cationic Solid Lipid NanoparticlesNarváez Narváez, David A.; Duarte Ruiz, María; Jiménez Lozano, Sandra; Moreno Castro, Cristina; Vargas, Ronny; Nardi Ricart, Anna; García Montoya, Encarna; Pérez Lozano, Pilar; Suñé Negre, Josep Mª; Hernández Munain, Cristina; Suñé, Carlos; Suñé Pou, Marc